Fifteen years of enzyme replacement therapy for mucopolysaccharidosis type VI (Maroteaux–Lamy syndrome): a case report

Name: Work Video:
Duration: 3 min 30 s
Isadora Andrade; River Ribeiro; Zumira Aparecida Carneiro; Roberto Giugliani; Catarina Pereira; Claudia Cozma; Daniel Grinberg; Lluı̈sa Vilageliu; Charles Marques Lourenço
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