Current Clinical Applications of In Vivo Gene Therapy with AAVs

Name: Work Video:
Duration: 3 min 30 s
Jerry R. Mendell; Samiah Al-Zaidy; Louise R. Rodino‐Klapac; Kimberly Goodspeed; Steven J. Gray; Christine N. Kay; Sanford L. Boye; Sanford L. Boye; Lindsey A. George; Stephanie Salabarria; Manuela Corti; Barry J. Byrne; Jacques P. Tremblay
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